PTC Therapeutics — Clinical Trials

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	PTC124 Genetic Disorders
		Phase 2b DMD/BMD Trial Sites
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PTC124 Genetic Disorders

PTC is currently developing PTC124, a novel, orally administered, small-molecule, investigational new drug for the treatment of genetic disorders in which a nonsense mutation is the cause of disease.

For more information on our clinical results, or PTC124, please visit the PTC124 page of our website.

PTC124 Genetic Disorders

PTC299 Oncology

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PTC124 FAQ

For answers to frequently asked questions about the Phase 2b DMD/BMD trial
click here.

Find trial centers

For a map of PTC124 Phase 2b trial sites for DMD/BMD please
click here.

Refer patients to trial

For physicians treating DMD patients interested in referring patients to the study, please complete the Referring Physician Survey.